Biomarkers in Sickle Cell Disease & Their Application to Gene Therapy
Time: 1:00 pm
day: Day One
• How can we use biomarkers to better collect data and characterize patients with sickle cell and thalassaemia?
• How to identify biomarkers already validated and collect information to document response to gene therapy
• Using the identification of good biomarkers to show future research needed to collect better data and design studies